Modulation of Immune Reaction in Hydrodynamic Gene Therapy for Hemophilia A

Mei Zhao, Yi Dan Sun, Mengdi Yin, Juan Juan Zhao, Si Ang Li, Guohua Li, Feng Zhang, Jing Xu, Fei Ying Meng, Beldon Zhang, Xin Yu Sun, Jian Ping Zhang, Tao Cheng, Xiao Bing Zhang

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)404-420
Number of pages17
JournalHuman Gene Therapy
Volume33
Issue number7-8
DOIs
StatePublished - Apr 2022

ASJC Scopus Subject Areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics

Keywords

  • CRISPR-Cas9
  • genome editing
  • hemophilia A
  • plasmids

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