Leveraging CRISPR-Cas9 for Accurate Detection of AAV-Neutralizing Antibodies: The AAV-HDR Method

Guohua Li, Saining Tian, Xinyu Sun, Mei Zhao, Feng Zhang, Jian Ping Zhang, Tao Cheng, Xiao Bing Zhang

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
JournalHuman Gene Therapy
DOIs
StateAccepted/In press - 2024
Externally publishedYes

ASJC Scopus Subject Areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics

Keywords

  • AAV homologous recombination (AAV-HDR)
  • AAV overexpression (AAV-OE)
  • AAV vector
  • AAV-neutralizing antibody
  • CRISPR–Cas9
  • NT50

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